Daybue: First and only FDA approved drug for Rett syndrome Daybue: First and only FDA approved drug for Rett syndrome,...
FDA
FDA delays 3-month update on Roktavian gene therapy for hemophilia A. Just when BioMarin considered its hemophilia A gene...
FDA approved 5 new drugs In February: 4 of which were orphan drugs FDA approved 5 new drugs In...
Milestone: FDA approves first human clinical trial of LNP-delivered in vivo CRISPR gene editing Milestone: FDA approves first human...
Musk Neuralink: Application of human trial is rejected by FDA due to big safety risk Musk Neuralink: Application of...
FDA approved the long-acting Altuviiiio therapy for the treatment of hemophilia A FDA approved the long-acting Altuviiiio therapy for...
